Workshop: Ensuring Success of Rare and Orphan Disease Drug Development

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AC Hotel San Francisco Airport/Oyster Point Waterfront

1333 Veterans Boulevard

South San Francisco, CA 94080

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Workshop: Ensuring Success of Rare and Orphan Disease Drug Development

Join us to get insights, expert guidance, and hear practical case studies that address the major challenges of rare disease drug development, from drug candidate early development, through regulatory strategy, trial design, patient engagement and market access.

The full day workshop agenda includes:

  • Understanding Current US and EU Regulations for Endpoint Design and Drug Approval

  • Patient Insights and Advocacy Groups

  • Designing Patient-Based Clinical Trials

  • Successful Rare Disease Trial Execution

  • Patient Engagement and Retention

  • Strategic Market Access and Reimbursement

Refreshments and Networking

Welcome refreshments and registration from 9:30 to 10:00. Lunch will be provided.

Additional details and speaker biographies are on our website.

Intended Audience

This workshop is intended for pharma and biotech professionals involved in rare disease development, including:

  • Medical Directors
  • Therapy Area Directors
  • Clinical Trial Directors/Managers
  • Regulatory Affairs
  • Market Access
  • Patient Advocacy Groups looking to set up registries and clinical trials

Registrations from vendors or other-third party organizations may be declined at the organiser's discretion.

Date and Time

Location

AC Hotel San Francisco Airport/Oyster Point Waterfront

1333 Veterans Boulevard

South San Francisco, CA 94080

View Map

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