$250 – $5,000

Translational Research Conference for the Management of NCLs

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The Westin Lombard Yorktown Center

70 Yorktown Shopping Center

Lombard, IL 60148

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On November 7th & 8th, we will assemble a group of the world's leading researchers in the Chicago area to discuss recent progress and future directions in translational research for all forms of Batten disease.

Batten disease refers to a family of progressive neurodegenerative disorders that are also known as the neuronal ceroid lipofuscinoses (NCLs). As a group, Batten disease is the most frequent neurodegenerative disease of childhood with a worldwide incidence of 1 per 14,000 to 1 per 67,000. All forms are monogenic, autosomal recessive disease that are characterized by the accumulation of lipopigments in lysosomes of cells throughout the body. They present early in childhood with a myriad of phenotypes including visual loss, seizures, cognitive impairment, language difficulty, and motor dysfunction. All forms are ultimately fatal.

Recent developments in translational research for these disorders have led to FDA approval of Brineura for treatment of CLN2 and gene therapy clinical trials for CLN6 and CLN3. The discovery of potential therapeutic approaches continue to lead us closer to more human clinical trials. Moreover, this conference aims to educate upon novel therapeutic strategies being explored outside the Batten disease research community that might have implications in the treatment of Batten disease.

Specific topics that will be covered at this conference include:

  • Current Barriers and Strategies in Gene Therapy
  • Current Topics in Small Molecule Drug Discovery and Delivery
  • Emerging Genetic and Cellular Approaches
  • Clinical Trial Design
  • Emerging Technologies for Patient Reported Outcomes

***Confirmed Speakers***

  • Jodi McBride, PhD | Assistant Professor, Oregon National Primate Research Center
  • Casey Maguire, PhD | Assistant Professor of Neurology, Harvard Medical School | Department of Nuerology, Massachusets General Hospital
  • May Khanna, PhD | Assistant Professor, Department of Pharmacology, The University of Arizona
  • Michelle Hastings, PhD | Associate Professor, Rosalind Franklin University of Medicine and Science

Opportunities to sponsor the event are available and we ask that you carefully consider this opportunity. Sponsors will be recognized in printed and electronic means at the conference.


Sponsorship levels include:

  • Platinum: $5000+ (Includes registration for two attendees)
  • Gold: $1500+ (Includes registration for two attendees)
  • Silver: $500+ (Includes registration for one attendee)



If you plan to sponsor the event, please use the Donation registration in place of Conference Attendee registration.

We hope you join us as we gather families, scientists, and industry experts to discuss the latest in therapeutic developments and preclinical/clinical study design with cross cutting applications for multiple forms of Batten disease.

If you have any questions prior to registration please contact:

Sarah at researchevents@sanfordhealth.org or Heather Dainiak at heatherdainiak@hotmail.com

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Date and Time

Location

The Westin Lombard Yorktown Center

70 Yorktown Shopping Center

Lombard, IL 60148

View Map

Refund Policy

Refunds up to 1 day before event

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